Awaiting FDA nod, Novartis touts latest data on gene therapy Zolgensma

As Novartis waits for FDA action on its gene therapy Zolgensma, expected this month, the company has rolled out yet another round of data on the spinal muscular atrophy treatment. Novartis’ AveXis, which developed the gene therapy, touted interim data through March 8 from a phase 1 study in Type 2 SMA patients, plus later-stage studies in Type 1 and presymptomatic SMA patients.
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